Investigating how RNA and protein processes affect frontotemporal dementia

RNA Surveillance and Protein Translation in FTD

NIH-funded research University of Arizona · NIH-10927336

This study is looking at how changes in a specific gene related to frontotemporal dementia can affect brain cells, and it hopes to find new ways to help people with this condition.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Arizona NIH-funded
Lab location1 site (Tucson, United States)
Project IDNIH-10927336 on NIH RePORTER

What this research studies

This research focuses on frontotemporal dementia (FTD), particularly a form associated with the FUS protein. It aims to understand how mutations in the FUS gene disrupt normal RNA surveillance and protein translation, leading to neuronal loss. The study will utilize both animal models and patient tissues to explore these mechanisms. By examining how these processes are altered in FTD, the research seeks to uncover potential therapeutic targets for this debilitating condition.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with frontotemporal dementia, especially those with FUS-related mutations.

Not a fit: Patients with forms of dementia unrelated to FUS mutations may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments that slow down or prevent neuronal loss in patients with frontotemporal dementia.

How similar studies have performed: Previous research has shown promising results in understanding the role of protein mislocalization in neurodegenerative diseases, suggesting that this approach could yield valuable insights.

Where this research is happening

Tucson, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Amyotrophic Lateral Sclerosis Motor Neuron Disease
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.