Investigating how mTOR signaling affects brain development in autism

Regulation of mTOR signaling in the developing cerebral cortex as a point of convergence for multiple autism risk factors

NIH-funded research Seattle Children's Hospital · NIH-11077352

This study is looking at how certain genetic changes might affect brain development and behavior in autism, and it hopes to find new ways to help improve brain function for those with autism and related challenges.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionSeattle Children's Hospital NIH-funded
Lab location1 site (Seattle, United States)
Project IDNIH-11077352 on NIH RePORTER

What this research studies

This research focuses on understanding the role of mTOR signaling in the developing brain, particularly how it relates to autism spectrum disorder (ASD) and intellectual disabilities. The study examines genetic mutations, specifically in the DYRK1A gene, that may lead to brain growth issues and behavioral deficits associated with ASD. By using mouse models, researchers aim to uncover the mechanisms behind these mutations and explore potential treatments that could enhance mTOR signaling to improve brain development and function. Patients may benefit from insights that could lead to targeted therapies for ASD.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with autism spectrum disorder, particularly those with known genetic mutations affecting mTOR signaling.

Not a fit: Patients without autism spectrum disorder or those whose conditions are unrelated to mTOR signaling may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments that improve brain development and cognitive function in individuals with autism.

How similar studies have performed: Previous research has shown promising results in understanding mTOR signaling in relation to autism, suggesting that this approach could lead to significant advancements in treatment.

Where this research is happening

Seattle, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions autism spectral disorderautism spectrum disorderAutistic Disorderautistic spectrum disorder
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.