Investigating how GABAA receptors fold and misfold in the brain

Understanding GABAA receptor protein folding and misfolding

NIH-funded research Case Western Reserve University · NIH-11161454

This study is looking into how certain changes in brain receptors can cause problems for people with epilepsy, with the goal of finding new ways to help those who don't respond well to current treatments.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionCase Western Reserve University NIH-funded
Lab location1 site (Cleveland, United States)
Project IDNIH-11161454 on NIH RePORTER

What this research studies

This research focuses on understanding the molecular mechanisms behind the misfolding of GABAA receptors, which are crucial for controlling brain activity. It aims to identify how genetic variations in these receptors lead to their dysfunction, particularly in patients with epilepsy. By studying the processes that cause these receptors to misfold and degrade, the research seeks to develop new therapeutic strategies to restore their function and improve treatment outcomes for patients resistant to current anti-seizure medications.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals with genetic forms of epilepsy linked to GABAA receptor dysfunction.

Not a fit: Patients with epilepsy not associated with GABAA receptor mutations may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments for epilepsy patients who do not respond to existing medications.

How similar studies have performed: Previous research has shown promise in correcting the function of misfolded GABAA receptors, indicating potential for success in this area.

Where this research is happening

Cleveland, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.