Investigating a new treatment target for a deadly childhood brain cancer

ATIC is a novel molecular target in diffuse intrinsic pontine glioma

NIH-funded research Emory University · NIH-11191212

This study is looking at a new way to fight a tough brain cancer called DIPG in kids by targeting a specific molecule that might help the tumors grow, with hopes of finding better treatments to help these children.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionEmory University NIH-funded
Lab location1 site (Atlanta, United States)
Project IDNIH-11191212 on NIH RePORTER

What this research studies

This research focuses on diffuse intrinsic pontine glioma (DIPG), a highly aggressive and currently incurable brain cancer in children. The team is exploring a novel molecular target called ATIC, which is involved in purine metabolism and may play a role in the growth of DIPG tumors. By using advanced techniques like metabolomics and CRISPR gene editing, the researchers aim to understand how inhibiting ATIC can affect tumor growth and survival in mouse models. The goal is to develop combination therapies that can overcome resistance to existing treatments and improve outcomes for affected children.

Who could benefit from this research

Good fit: Ideal candidates for this research are children diagnosed with diffuse intrinsic pontine glioma.

Not a fit: Patients with other types of brain tumors or those who are not diagnosed with DIPG may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new therapeutic strategies that significantly improve survival rates for children with DIPG.

How similar studies have performed: While the approach of targeting molecular pathways in DIPG is relatively novel, preliminary studies have shown promise in identifying effective treatment strategies.

Where this research is happening

Atlanta, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.