Injecting stem cells to help children with a serious heart condition

1/2 Allogeneic Human Mesenchymal Stem Cell (MSC) Injection in Patients with Hypoplastic Left Heart Syndrome: A Phase IIb Clinical Trial

NIH-funded research Lurie Children's Hospital of Chicago · NIH-10890142

This study is looking at whether special stem cells can help improve heart function in children with Hypoplastic Left Heart Syndrome, a serious heart condition, and it's designed to find new treatment options for these kids.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionLurie Children's Hospital of Chicago NIH-funded
Lab location1 site (Chicago, United States)
Project IDNIH-10890142 on NIH RePORTER

What this research studies

This research investigates the use of allogeneic human mesenchymal stem cells (MSCs) to treat children with Hypoplastic Left Heart Syndrome (HLHS), a complex congenital heart defect. The study involves a Phase IIb clinical trial where MSCs are injected into patients to assess their effectiveness in improving heart function. The research is conducted across multiple clinical sites, focusing on managing patient enrollment and overseeing the clinical design. By building on previous studies, this trial aims to provide a new treatment option for children who often face high mortality rates due to heart complications.

Who could benefit from this research

Good fit: Ideal candidates for this research are infants and young children diagnosed with Hypoplastic Left Heart Syndrome.

Not a fit: Patients with other congenital heart defects or those who are not within the age range of 0-11 years may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to improved heart function and survival rates for children with Hypoplastic Left Heart Syndrome.

How similar studies have performed: Previous studies using stem cell therapies in similar contexts have shown promise, suggesting potential for success in this trial.

Where this research is happening

Chicago, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.