Improving treatment for acute myeloid leukemia with IDH mutations

Project 1: Increasing therapeutic efficacy in isocitrate dehydrongenase (IDH)–mutant acute myeloid leukemia (AML)

NIH-funded research Sloan-Kettering Inst Can Research · NIH-10862892

This study is looking to improve treatments for people with acute myeloid leukemia who have certain gene mutations, by figuring out why some don’t respond to current medications and testing new combination therapies that could work better for them.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionSloan-Kettering Inst Can Research NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-10862892 on NIH RePORTER

What this research studies

This research focuses on enhancing the effectiveness of treatments for patients with acute myeloid leukemia (AML) who have specific mutations in the IDH1 and IDH2 genes. By analyzing patient samples and conducting preclinical studies, the team aims to identify why some patients do not respond to existing IDH inhibitors and to develop new combination therapies that could improve outcomes. The research includes clinical trials that will test these new approaches in genetically defined patient groups, providing a tailored treatment strategy based on individual genetic profiles.

Who could benefit from this research

Good fit: Ideal candidates for this research are patients diagnosed with acute myeloid leukemia who have mutations in the IDH1 or IDH2 genes.

Not a fit: Patients without IDH1 or IDH2 mutations or those with other types of leukemia may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatment options for patients with IDH-mutant acute myeloid leukemia, potentially improving survival rates and quality of life.

How similar studies have performed: Previous research has shown promising results with IDH inhibitors in treating relapsed/refractory IDH-mutant AML, indicating that this approach has potential for further success.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.