Improving predictions of side effects from azathioprine treatment

A Personalized Medicine Approach to Improve the Prediction of Azathioprine Toxicity

NIH-funded research University of Miami School of Medicine · NIH-10783440

This study is looking at how your genes might help doctors figure out if you could have serious side effects from the medication azathioprine, which is used for inflammatory conditions, so they can tailor your treatment to keep you safe and healthy.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Miami School of Medicine NIH-funded
Lab location1 site (Coral Gables, United States)
Project IDNIH-10783440 on NIH RePORTER

What this research studies

This research investigates how genetic factors can help predict which patients are at risk for serious side effects from azathioprine, a medication used to treat inflammatory conditions. By analyzing genetic variants beyond the commonly used TPMT testing, the study aims to develop a more comprehensive genetic risk score that can identify patients who may experience myelosuppression or pancreatitis. The research utilizes large biobanks to gather data and improve the accuracy of predictions, ultimately aiming to personalize treatment plans for better safety and efficacy.

Who could benefit from this research

Good fit: Ideal candidates for this research are patients who are prescribed azathioprine for inflammatory conditions and may be at risk for its side effects.

Not a fit: Patients who are not prescribed azathioprine or those who do not have genetic variations associated with azathioprine toxicity may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could significantly reduce the incidence of severe side effects from azathioprine, leading to safer treatment options for patients.

How similar studies have performed: Other research has shown promise in using genetic testing to predict drug toxicity, suggesting that this approach could lead to meaningful advancements in personalized medicine.

Where this research is happening

Coral Gables, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.