Improving genome editing techniques for treating genetic diseases
Translational Coordination and Dissemination Center for the SCGE Consortium
This study is working on improving gene editing tools to fix genetic mutations that cause diseases, with the goal of creating better treatment options for patients like you.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Medical College of Wisconsin NIH-funded |
| Lab location | 1 site (Milwaukee, United States) |
| Project ID | NIH-11132891 on NIH RePORTER |
What this research studies
This research focuses on advancing genome editing technologies to correct disease-causing mutations. The project aims to translate laboratory findings into clinical applications through a coordinated effort among various initiatives. It involves building communication platforms, collecting and distributing data, and fostering collaborations within the scientific community. Patients may benefit from improved treatment options as these technologies are developed and refined.
Who could benefit from this research
Good fit: Ideal candidates for participation are individuals with genetic diseases linked to known mutations that can be targeted by genome editing.
Not a fit: Patients with genetic conditions that do not have identified mutations or are not amenable to genome editing may not benefit from this research.
Why it matters
Potential benefit: If successful, this research could lead to more effective treatments for genetic diseases caused by specific mutations.
How similar studies have performed: Previous research in genome editing has shown promising results, indicating that this approach has the potential for significant breakthroughs in treatment.
Where this research is happening
Milwaukee, United States
- Medical College of Wisconsin — Milwaukee, United States (Active)
Researchers
- Principal investigator: Dwinell, Melinda R — Medical College of Wisconsin
- Study coordinator: Dwinell, Melinda R
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page below.