Improving genome editing techniques for treating genetic diseases
Official title: Translational Coordination and Dissemination Center for the SCGE Consortium
Funded at Medical College of Wisconsin · NIH-11132891 · Data updated 2026-11-12
This study is working on improving gene editing tools to fix genetic mutations that cause diseases, with the goal of creating better treatment options for patients like you.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Medical College of Wisconsin NIH-funded |
| Lab location | 1 site (Milwaukee, United States) |
| Project start | June 1, 2023 |
| Project end | May 31, 2028 |
| Funding year | 2025 |
| Award (this year) | $1,752,114 |
| NIH project number | 5U24HL168712-03 |
| Project ID | NIH-11132891 on NIH RePORTER |
Who could benefit from this research
✓Could help
Ideal candidates for participation are individuals with genetic diseases linked to known mutations that can be targeted by genome editing.
✕Less likely to help
Patients with genetic conditions that do not have identified mutations or are not amenable to genome editing may not benefit from this research.
What this research studies
This research focuses on advancing genome editing technologies to correct disease-causing mutations. The project aims to translate laboratory findings into clinical applications through a coordinated effort among various initiatives. It involves building communication platforms, collecting and distributing data, and fostering collaborations within the scientific community. Patients may benefit from improved treatment options as these technologies are developed and refined.
Why it matters
Potential benefit: If successful, this research could lead to more effective treatments for genetic diseases caused by specific mutations.
How similar studies have gone: Previous research in genome editing has shown promising results, indicating that this approach has the potential for significant breakthroughs in treatment.
Where this research is happening
-
Medical College of Wisconsin
Milwaukee, United States Active
Researchers
- Principal investigator: Dwinell, Melinda R — Medical College of Wisconsin
- Study coordinator: Dwinell, Melinda R
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.