Identifying genetic defects that cause severe immune deficiencies in children

Curation of genetic defects causing combined immunodeficiency and infections in children

['FUNDING_OTHER'] · BAYLOR COLLEGE OF MEDICINE · NIH-10669125

This study is looking at the genetic causes of severe combined immune deficiencies (SCID) in kids, so doctors can better understand how to treat them with options like gene therapy or bone marrow transplants, helping to keep them healthy and safe from infections.

Quick facts

Phase['FUNDING_OTHER']
Study typeNih_funding
SexAll
SponsorBAYLOR COLLEGE OF MEDICINE (nih funded)
Locations1 site (HOUSTON, UNITED STATES)
Trial IDNIH-10669125 on ClinicalTrials.gov

What this research studies

This research focuses on understanding the genetic defects that lead to severe combined immune deficiencies (SCID) in children, which make them highly susceptible to infections. By analyzing genetic information from newborns identified through screening, the research aims to clarify the significance of various genetic variants. This will help healthcare providers make informed decisions about the most effective treatments, such as gene therapy or bone marrow transplants, ensuring timely and appropriate care for affected children.

Who could benefit from this research

Good fit: Ideal candidates for this research are newborns diagnosed with severe combined immune deficiencies or those identified through newborn screening programs.

Not a fit: Patients with immune deficiencies not caused by genetic defects or those diagnosed after the newborn screening period may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more accurate diagnoses and tailored treatments for children with severe immune deficiencies, improving their health outcomes.

How similar studies have performed: Previous research has shown success in identifying genetic causes of immune deficiencies, indicating that this approach has the potential for significant advancements.

Where this research is happening

HOUSTON, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.