How tiny cell antennae control Hedgehog signals

Protein dynamics underlying cilium-dependent Hedgehog signaling

['FUNDING_R01'] · MASSACHUSETTS GENERAL HOSPITAL · NIH-11146667

Researchers are using advanced lab techniques to understand how tiny cell antennae called primary cilia control Hedgehog signals that affect development and some cancers.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorMASSACHUSETTS GENERAL HOSPITAL (nih funded)
Locations1 site (BOSTON, UNITED STATES)
Trial IDNIH-11146667 on ClinicalTrials.gov

What this research studies

This lab project focuses on primary cilia, the small antenna-like structures on cells that are essential for Hedgehog signaling important in development and certain tumors. The team will rebuild key parts of the Hedgehog pathway from purified proteins, use single-molecule imaging to watch how individual proteins behave, and run biochemical and cell-based assays to see how complexes form at the base and tip of cilia. By linking molecular behavior to cellular responses, they aim to explain how defects in cilia-based signaling lead to birth defects and cancers. The work is conducted in the lab at Massachusetts General Hospital using cell systems and biochemical methods rather than a clinical trial.

Who could benefit from this research

Good fit: Although this grant does not enroll patients directly, its findings are most relevant to people with basal cell carcinoma, medulloblastoma, or congenital skeletal and craniofacial malformations linked to Hedgehog signaling.

Not a fit: People with conditions unrelated to Hedgehog signaling, such as routine metabolic or cardiovascular diseases, are unlikely to see direct benefits from this work.

Why it matters

Potential benefit: If successful, this research could reveal mechanisms behind congenital malformations and cancers driven by Hedgehog pathway errors, pointing to new targets for diagnostics or therapies.

How similar studies have performed: Many studies have mapped the proteins in the Hedgehog pathway and used cellular imaging, but fully reconstituting cilia-based signaling and watching single-molecule interactions is a newer and not-yet-established approach.

Where this research is happening

BOSTON, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.