How the protein FGF21 may link RPE cell energy failure to vision loss

FGF21 as a mediator of RPE mitochondrial dysfunction

NIH-funded research Stanford University · NIH-11285462

This project looks at whether changing levels of the protein FGF21 can prevent or reduce retinal cell damage that contributes to age-related macular degeneration.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionStanford University NIH-funded
Lab location1 site (Stanford, United States)
Project IDNIH-11285462 on NIH RePORTER

What this research studies

The team uses mouse models with targeted mitochondrial damage in the retinal pigment epithelium (RPE) to see how FGF21 signals between RPE cells and photoreceptors. They will raise or lower FGF21 levels genetically and with treatments, then measure retinal structure and function over time. Lab studies on RPE cells will probe the molecular steps by which FGF21 spreads stress signals to neighboring retinal tissue. Together these approaches aim to reveal whether FGF21 drives damage and whether blocking or replacing it can protect vision.

Who could benefit from this research

Good fit: People with early or intermediate age-related macular degeneration or inherited retinal conditions linked to mitochondrial problems would be most connected to this line of work.

Not a fit: Patients with unrelated eye conditions or those with very advanced, end-stage vision loss are unlikely to benefit directly from these preclinical experiments.

Why it matters

Potential benefit: If successful, this work could identify FGF21 as a new target to slow or prevent photoreceptor loss in AMD and related retinal diseases.

How similar studies have performed: Prior lab studies in other tissues and early mouse work suggest FGF21 can affect cell survival, but translating this to human retinal therapy is still unproven.

Where this research is happening

Stanford, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.