How the mitochondrial protein GDAP1 affects Alzheimer's disease

Role of mitochondrial GDAP1 in Alzheimer's disease

NIH-funded research University of Pittsburgh at Pittsburgh · NIH-11317200

This project looks at whether a brain protein called GDAP1 helps protect nerve cells from harmful molecules in people with Alzheimer's disease.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Pittsburgh at Pittsburgh NIH-funded
Lab location1 site (Pittsburgh, United States)
Project IDNIH-11317200 on NIH RePORTER

What this research studies

Researchers will compare levels of GDAP1 in brain tissue and gene data from people with Alzheimer's and people without dementia. In the lab they will study how GDAP1 binds and neutralizes a toxic product of lipid damage called 4-HNE and how that interaction affects mitochondrial health. The team will use cell and molecular experiments and analyses of human brain datasets to test whether lower GDAP1 makes neurons more vulnerable to oxidative damage. Findings will come from work done at the University of Pittsburgh and partner datasets.

Who could benefit from this research

Good fit: Adults diagnosed with Alzheimer's disease or related dementia, and older adults who can provide brain-related biospecimens or participate in comparison cohorts, would be the most relevant participants.

Not a fit: People without Alzheimer's, younger individuals, or anyone seeking immediate symptom relief are unlikely to get direct benefit from this basic and translational research.

Why it matters

Potential benefit: If true, the work could point to new ways to protect brain cells in Alzheimer's or lead to therapies that boost GDAP1 function or limit 4-HNE damage.

How similar studies have performed: Prior work linking oxidative damage and mitochondrial proteins has suggested targets for neuroprotection, but focusing specifically on GDAP1 in Alzheimer's is a newer and less-tested approach.

Where this research is happening

Pittsburgh, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.