How the GLUT1 glucose transporter affects early brain growth and development

Determining the Role of Glucose Transporter 1 in Neural Development and Disease

NIH-funded research Weill Medical Coll of Cornell Univ · NIH-11308725

This project will look at how problems with the GLUT1 protein in early brain cells may lead to conditions like GLUT1 deficiency, seizures, autism, and ADHD.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionWeill Medical Coll of Cornell Univ NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11308725 on NIH RePORTER

What this research studies

Researchers will use both mouse experiments and human cell models to reduce or remove GLUT1 in neural progenitor (early brain) cells and watch how those cells grow, divide, and become neurons. They will measure cell proliferation, cell-cycle changes, fate decisions, and metabolic activity using imaging, single-cell analyses, and biochemical assays. The mouse work shows effects in a developing brain, while human-derived cells help link findings to human GLUT1-Deficiency Syndrome and related neurodevelopmental conditions. Together these approaches aim to reveal when and how GLUT1 problems disrupt brain development.

Who could benefit from this research

Good fit: People with GLUT1-Deficiency Syndrome, early-onset unexplained seizures, developmental delay, or related neurodevelopmental conditions (or families willing to donate blood or cells) would be most relevant to this work.

Not a fit: Patients whose conditions are unrelated to glucose transport or who have only adult-onset neurological issues are unlikely to see direct benefit from this project.

Why it matters

Potential benefit: If successful, this work could clarify how GLUT1-related problems cause developmental brain disorders and point to earlier diagnosis or new treatment strategies.

How similar studies have performed: Previous research has linked GLUT1 problems to neurological disease and shown benefits from metabolic therapies like the ketogenic diet, but using NPC-specific GLUT1 loss in combined mouse and human cell models is a newer approach.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Attention Deficit DisorderAttention deficit hyperactivity disorderAutistic Disorder
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.