How sperm-producing stem cells are controlled by epigenetics

Epigenetic control of spermatogonial stem cell self-renewal

NIH-funded research University of Pennsylvania · NIH-11319011

This project looks at how an epigenetic protein called DOT1L helps sperm-making stem cells keep renewing, with the goal of informing treatments for men with low or absent sperm production.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Pennsylvania NIH-funded
Lab location1 site (Philadelphia, United States)
Project IDNIH-11319011 on NIH RePORTER

What this research studies

Researchers will work mostly in animal models and cell cultures to learn how DOT1L, an epigenetic enzyme, affects the balance between self-renewal and differentiation of spermatogonial stem cells that make sperm. They will use genetic tools and chemical inhibitors of DOT1L, together with genomic assays such as ATAC-seq, to identify the genes and pathways changed when DOT1L activity is altered. Functional approaches like in vitro stem cell cultures and transplantation experiments will test whether changes rescue or impair sperm-producing capacity. The aim is to find molecular targets that could later be developed into therapies to restore sperm production in men.

Who could benefit from this research

Good fit: Men with problems producing sperm (non-obstructive azoospermia or unexplained low sperm counts) would be the most relevant group for future treatments or clinical studies arising from this work.

Not a fit: This research is unlikely to help people whose infertility is caused by blocked sperm ducts, partner-related infertility, or conditions that destroy all sperm-producing cells permanently.

Why it matters

Potential benefit: If successful, this work could point to new ways to restore or improve sperm production and help some men with infertility father children.

How similar studies have performed: Prior laboratory and animal studies have identified genes that control spermatogonial stem cells and enabled experimental stem-cell transplantation in animals, but targeting DOT1L and similar epigenetic regulators is a more recent and less-tested approach.

Where this research is happening

Philadelphia, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.