How SCN2A changes affect brain activity and social behavior in autism

Neuronal and Behavioral Deficits Associated with Scn2a Deficiency in Autism Spectrum Disorder

['FUNDING_R01'] · PURDUE UNIVERSITY · NIH-11378873

This work looks at whether SCN2A gene changes disrupt brain cell activity and social behavior in autism and whether genetic or drug fixes can improve those behaviors.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorPURDUE UNIVERSITY (nih funded)
Locations1 site (WEST LAFAYETTE, UNITED STATES)
Trial IDNIH-11378873 on ClinicalTrials.gov

What this research studies

Researchers use a mouse model that mimics SCN2A deficiency found in some people with autism. They record brain cell activity in the prefrontal cortex using brain-slice patch-clamp techniques and Neuropixels in vivo probes to measure neuronal firing and excitation/inhibition balance. The team will test genetic 'rescue' approaches and pharmacological treatments to see if normalizing excitation/inhibition balance reduces anxiety-like behaviors and improves social interactions. Results could point researchers toward treatments aimed at SCN2A-related autism.

Who could benefit from this research

Good fit: People with autism who have a known damaging SCN2A variant (and their families) are the most directly relevant group.

Not a fit: People with autism who do not carry SCN2A variants or whose symptoms arise from different mechanisms may not benefit directly from these findings.

Why it matters

Potential benefit: Could point to genetic or drug strategies that restore normal brain signaling and improve social behaviors in people with SCN2A-related autism.

How similar studies have performed: Previous animal studies have linked SCN2A loss to social deficits and altered excitation/inhibition balance, but translating these findings into effective human therapies remains early and experimental.

Where this research is happening

WEST LAFAYETTE, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.