How retinal cells might be reprogrammed to replace lost neurons

Mechanisms regulating the plasticity of postmitotic cells in mammalian retina

NIH-funded research Stanford University · NIH-11082304

This research tries to find whether switching on specific genes can help adult retinal cells change into the nerve cells needed to replace those lost in retinal diseases.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionStanford University NIH-funded
Lab location1 site (Stanford, United States)
Project IDNIH-11082304 on NIH RePORTER

What this research studies

Researchers analyzed gene activity in newly born retinal cells to find genes that help cells decide their final type. They use single-cell RNA sequencing data, retroviral-based genetic tools, and light-sheet microscopy to study these genes' roles in living tissue. A focus is on the transcription factor Myt1, which helps newborn retinal cells become neurons rather than glia during development. The team will test whether the same genes can coax adult retinal cells to reprogram into useful neuron types that are damaged in disease.

Who could benefit from this research

Good fit: This work is ultimately aimed at people with retinal degenerative diseases (for example age-related macular degeneration or retinitis pigmentosa), although the current project is preclinical.

Not a fit: People whose vision loss is due to non-retinal causes (such as optic nerve injury or cortical blindness) are unlikely to benefit from these retinal reprogramming approaches.

Why it matters

Potential benefit: If successful, this work could point to ways to regenerate retinal neurons from a patient’s own cells and potentially restore vision lost to retinal disease.

How similar studies have performed: Animal and lab studies have shown that changing key genes can reprogram retinal cells, but applying Myt1-driven reprogramming to adult mammalian retina is a newer and less-tested approach.

Where this research is happening

Stanford, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Candidate Disease Gene
Last reviewed 2026-06-09 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.