How granule cells in the cerebellum develop

Regulatory mechanisms of cerebellar lineage development

['FUNDING_R01'] · VANDERBILT UNIVERSITY · NIH-11327321

Researchers are learning how tiny cerebellar granule cells form and change early in life to better understand conditions like autism and cerebellar hypoplasia.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorVANDERBILT UNIVERSITY (nih funded)
Locations1 site (Nashville, UNITED STATES)
Trial IDNIH-11327321 on ClinicalTrials.gov

What this research studies

This project studies the molecular switches that let granule cell precursors stop dividing and become mature granule cells, focusing on genes such as Atoh1, Ccnd1, Sin3A, and Insm1. The team uses laboratory models and molecular and epigenetic techniques to see how those genes are turned on and off during embryonic and early postnatal development. They link these basic mechanisms to human risks like prematurity and developmental brain differences that can lead to cerebellar hypoplasia and features of autism. The work is preclinical and aims to find steps in development that could become targets for future tests or therapies.

Who could benefit from this research

Good fit: This work would be most relevant to families affected by cerebellar hypoplasia, people with autism linked to cerebellar differences, and parents of very preterm infants.

Not a fit: Because this is lab-based basic research rather than a clinical treatment trial, people seeking immediate medical therapies are unlikely to receive direct benefit.

Why it matters

Potential benefit: If successful, this work could point to new ways to prevent or treat cerebellar growth problems and related developmental symptoms in infants and children.

How similar studies have performed: Prior studies have shown Atoh1 and Ccnd1 shape granule cell development, but the role of Sin3A and Insm1 in epigenetic silencing and timely differentiation is a newer and early-stage finding.

Where this research is happening

Nashville, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Autistic Disorder

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.