How GLIS3 helps make and protect insulin-producing pancreatic beta cells

Role of GLIS3 in Human Pancreatic Beta Cell Generation, Survival and Proliferation

NIH-funded research Weill Medical Coll of Cornell Univ · NIH-11249155

This project looks at whether changing a gene called GLIS3 can improve how human insulin-making beta cells are produced, survive, and grow for people with adult-onset diabetes.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionWeill Medical Coll of Cornell Univ NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11249155 on NIH RePORTER

What this research studies

Researchers will use human embryonic stem cells engineered to carry diabetes-linked GLIS3 variants or to lack GLIS3, then guide those cells to become pancreatic beta-like cells in the lab. They will compare how well these engineered cells form, survive, and multiply and will profile gene activity using tools such as ATAC-seq. The team will also test a TGFβ-blocking compound that in early work reduced cell death in GLIS3-deficient beta-like cells. The work aims to pinpoint molecular steps that could be targeted to improve beta cell health in diabetes.

Who could benefit from this research

Good fit: Adults with adult-onset (type 2) diabetes or people known to carry GLIS3-related mutations are the most relevant candidates to follow or to be asked to provide samples for related studies.

Not a fit: People whose diabetes is unrelated to GLIS3 or those seeking immediate clinical treatments are unlikely to get direct benefit from this laboratory-focused work.

Why it matters

Potential benefit: If successful, this work could point to new ways to protect or replace insulin-producing beta cells, helping people with diabetes need less insulin and avoid complications.

How similar studies have performed: Earlier lab studies link GLIS3 to beta cell formation and show a TGFβ inhibitor can reduce cell death in GLIS3-deficient cells, but clinical benefit in patients remains unproven.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Adult-Onset Diabetes Mellitus
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.