How GDNF may protect the liver from fat buildup

Mechanism of GDNF Regulation of Hepatic Steatosis

['FUNDING_OTHER'] · VETERANS HEALTH ADMINISTRATION · NIH-11224040

This project looks at whether a protein called GDNF helps liver cells avoid fat buildup and damage in people with non-alcoholic fatty liver disease.

Quick facts

Phase['FUNDING_OTHER']
Study typeNih_funding
SexAll
SponsorVETERANS HEALTH ADMINISTRATION (nih funded)
Locations1 site (Decatur, UNITED STATES)
Trial IDNIH-11224040 on ClinicalTrials.gov

What this research studies

Researchers are studying how the protein GDNF affects liver cells using a mix of approaches including human liver tissue, lab-grown human liver cells, and mouse models that overproduce GDNF. They measure processes that clear damaged cell parts (autophagy/mitophagy), track cell-death signals (apoptosis), and monitor related proteins like Sirt3 and GFRα-1. The team will map the signaling steps by which GDNF might reduce liver fat and prevent injury. Findings aim to explain why GDNF levels are lower in fatty and fibrotic human livers and how boosting GDNF pathways could protect the liver.

Who could benefit from this research

Good fit: Ideal candidates for any future clinical work based on this project would be adults with or at high risk for non-alcoholic fatty liver disease, especially those with obesity or metabolic syndrome.

Not a fit: People whose liver disease is primarily caused by alcohol, viral hepatitis, or who already have advanced cirrhosis may not benefit from findings focused on NAFLD mechanisms.

Why it matters

Potential benefit: If successful, this work could point to new ways to prevent or slow non-alcoholic fatty liver disease and reduce liver injury in people at risk.

How similar studies have performed: Early animal and cell studies from this group and others show promising protective effects of GDNF, but benefits in people have not yet been proven.

Where this research is happening

Decatur, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Cellular injury

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.