How DNA 'demethylation' controls light-sensing cells and links to inherited vision loss

The role of the TET-dependent DNA demethylation pathway in photoreceptor development and pathology

['FUNDING_R01'] · UNIVERSITY OF MIAMI SCHOOL OF MEDICINE · NIH-11143771

This work looks at whether a DNA-editing process called TET-dependent demethylation helps photoreceptor cells develop and whether its failure can lead to retinitis pigmentosa and related inherited vision loss.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorUNIVERSITY OF MIAMI SCHOOL OF MEDICINE (nih funded)
Locations1 site (CORAL GABLES, UNITED STATES)
Trial IDNIH-11143771 on ClinicalTrials.gov

What this research studies

From a patient's perspective, researchers will examine chemical tags on DNA that switch photoreceptor genes on and off during eye development. They will compare human retinal tissue and mouse models to see when and where those tags are removed and how that affects gene activity. The team will manipulate the TET demethylation pathway in lab models to test whether failed demethylation can silence critical photoreceptor genes and cause cell dysfunction or death. Results may clarify non‑mutation causes of inherited photoreceptor diseases and guide future therapies.

Who could benefit from this research

Good fit: People with inherited photoreceptor disorders such as retinitis pigmentosa, or those interested in contributing clinical samples for vision research, are the most relevant participants for related sample-collection or future clinical follow-ups.

Not a fit: Patients whose vision loss is due to unrelated conditions like age-related macular degeneration, glaucoma, or trauma are unlikely to benefit directly from this project.

Why it matters

Potential benefit: If successful, this work could reveal epigenetic causes of inherited photoreceptor loss and point to new ways to prevent or reverse vision decline.

How similar studies have performed: Previous studies have shown DNA methylation changes during retinal development, but applying TET-focused epigenetic mechanisms to explain or treat photoreceptor dystrophies is relatively new and not yet clinically proven.

Where this research is happening

CORAL GABLES, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.