How 22q11 genes shape brain development and adult brain connections

Regulation of 22q11 Genes in Embryonic and Adult Forebrain

NIH-funded research Virginia Polytechnic Inst and St Univ · NIH-11135477

This project looks at how losing 22q11 genes changes specific brain cells and their wiring, which may underlie conditions like autism and other neurodevelopmental disorders.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionVirginia Polytechnic Inst and St Univ NIH-funded
Lab location1 site (Blacksburg, United States)
Project IDNIH-11135477 on NIH RePORTER

What this research studies

The researchers use mouse models that carry the same 22q11.2 deletion found in people to follow how certain neurons called layer 2/3 projection neurons grow and connect across the forebrain. They examine cell growth, the balance of excitatory and inhibitory synapses, mitochondrial oxidative stress, and changes in gene and protein activity. The team combines genetic manipulation, electrophysiology, transcriptomics, proteomics, and behavioral testing from development into adulthood. The aim is to explain why circuit disconnection and variable behaviors occur in 22q11.2 deletion syndrome.

Who could benefit from this research

Good fit: People with a confirmed 22q11.2 deletion, especially those experiencing autism, anxiety, or cognitive difficulties, would be most relevant for related clinical follow-up or future trials.

Not a fit: People without a 22q11.2 deletion or whose symptoms come from unrelated causes are unlikely to receive direct benefit from this basic research.

Why it matters

Potential benefit: If successful, this work could reveal cellular and molecular targets to prevent or treat brain-circuit problems in people with 22q11.2 deletion syndrome.

How similar studies have performed: Previous mouse studies of 22q11DS have shown impaired neuron growth and mitochondrial stress, supporting this line of work, but translating findings into human treatments remains early.

Where this research is happening

Blacksburg, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions 22q11 Chromosomal Microdeletion Syndrome22q11 Deletion Syndrome22q11.2 deletion syndrome
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.