Gene editing to target HIV hiding in the body and brain

Broad-spectrum HIV gene editing strategies in peripheral and brain reservoirs

['FUNDING_R01'] · DREXEL UNIVERSITY · NIH-11256727

This work builds gene‑editing tools intended to remove or disable hidden HIV for people living with HIV, including virus hiding in the brain.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorDREXEL UNIVERSITY (nih funded)
Locations1 site (PHILADELPHIA, UNITED STATES)
Trial IDNIH-11256727 on ClinicalTrials.gov

What this research studies

This project develops CRISPR‑Cas9 guide RNAs designed to find and cut HIV DNA that persists in infected cells across body compartments, including the brain. The team uses a patented computational pipeline to pick guides that work across many HIV strains while minimizing the chance of cutting human genes. Guides are tested in cells and tissue/animal models to measure how well they edit viral DNA, how safe they are (off‑target effects), and whether they can reach brain reservoir cells. Findings are intended to support future clinical approaches for people living with HIV.

Who could benefit from this research

Good fit: People living with HIV who are stable on antiretroviral therapy and interested in experimental cure research would be the most likely candidates for future participation.

Not a fit: People without HIV or those who are not suitable for gene‑therapy approaches (for example with uncontrolled infections or certain medical conditions) would not be expected to benefit.

Why it matters

Potential benefit: If successful, this approach could reduce or eliminate latent HIV reservoirs and move toward a functional cure that reduces or ends the need for lifelong therapy.

How similar studies have performed: CRISPR approaches have reduced HIV DNA in cells and animal models, but no CRISPR‑based cure has yet been proven safe and effective in people.

Where this research is happening

PHILADELPHIA, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Acquired Immune Deficiency Syndrome Virus, Acquired Immunodeficiency Syndrome Virus

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.