Finding ways to identify people for early genetic therapies

Developing strategies to identify candidate individuals for early genetic therapies

NIH-funded research Duke University · NIH-10980623

This study is looking to make it easier for people to find out if they might benefit from genetic treatments before having a baby or during pregnancy, so they can get the right care sooner and improve their health.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionDuke University NIH-funded
Lab location1 site (Durham, United States)
Project IDNIH-10980623 on NIH RePORTER

What this research studies

This research focuses on improving the identification of individuals who may benefit from early genetic therapies. It aims to enhance the process of genetic diagnosis either before conception or during pregnancy, which can lead to timely treatment options. By refining guidelines for preconception carrier screening and utilizing large biobanks, the study seeks to ensure that more individuals receive appropriate genetic testing. This could ultimately allow for earlier interventions that may improve health outcomes for affected individuals.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals planning to conceive or those who are pregnant, particularly those with a family history of genetic disorders.

Not a fit: Patients who are not planning to conceive or who are not pregnant may not receive any benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to earlier diagnoses and treatments for genetic conditions, improving health outcomes for patients.

How similar studies have performed: Previous research has shown promise in improving genetic screening processes, indicating that this approach could be effective.

Where this research is happening

Durham, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Acid Maltase Deficiency Disease
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.