Finding New Treatments for Childhood Leukemia

NCI Pediatric In Vivo Testing Program - Leukemia

NIH-funded research University of New South Wales · NIH-11127479

This research aims to discover more effective medicines for children with aggressive or hard-to-treat acute lymphoblastic leukemia (ALL).

Quick facts

Grant typeU01 cooperative agreement
Study typeNIH-funded research
Funding institutionUniversity of New South Wales NIH-funded
Lab location1 site (Sydney, Australia)
Project IDNIH-11127479 on NIH RePORTER

What this research studies

Our goal is to improve treatment options for children facing aggressive or drug-resistant acute lymphoblastic leukemia. We do this by carefully testing new medicines in advanced laboratory models that closely mimic the disease in patients. These models, called patient-derived xenografts, are created from actual patient samples and grown in special mice, allowing us to see how new drugs might work before they are given to children. This helps us identify the most promising drugs to move forward into clinical trials, maximizing the chances of finding better cures.

Who could benefit from this research

Good fit: This preclinical research is designed to benefit future pediatric patients with acute lymphoblastic leukemia, particularly those whose disease is aggressive or has not responded to current treatments.

Not a fit: Patients currently undergoing treatment or those whose leukemia is well-controlled may not directly benefit from this early-stage drug discovery work.

Why it matters

Potential benefit: If successful, this work could lead to the discovery and prioritization of new, more effective drugs for children with acute lymphoblastic leukemia, especially those with aggressive or resistant forms of the disease.

How similar studies have performed: Preclinical testing programs using patient-derived models have shown promise in identifying effective treatments for various cancers, though each new drug candidate is unique.

Where this research is happening

Sydney, Australia

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.