Finding genes that cause pituitary and hypothalamus birth defects

Discovery Pipeline for Genetic Defects in Hypothalamic-pituitary Development Using International Mouse Phenotyping Consortium Mice

['FUNDING_R01'] · UNIVERSITY OF MICHIGAN AT ANN ARBOR · NIH-11345195

Researchers are using mouse models to find genes that lead to congenital pituitary and hypothalamic problems that cause hormone deficiencies in children and adults.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorUNIVERSITY OF MICHIGAN AT ANN ARBOR (nih funded)
Locations1 site (ANN ARBOR, UNITED STATES)
Trial IDNIH-11345195 on ClinicalTrials.gov

What this research studies

This project examines knockout mice that die before or shortly after birth and show malformations of the hypothalamus or pituitary gland to pinpoint the underlying genes. The team prioritized 18 mouse lines with clear developmental defects and will perform detailed imaging and tissue analyses to map how each genetic change alters organ formation. Genes are grouped by function (for example, epigenetic regulators or cilia components) to identify common pathways that could explain similar human birth defects. The goal is to expand the list of known genetic causes so more patients with congenital hypopituitarism can receive a molecular diagnosis.

Who could benefit from this research

Good fit: People born with congenital hypopituitarism or unexplained pituitary hormone deficiencies, especially those with midline birth defects, are the group most likely to benefit from expanded genetic findings.

Not a fit: Patients with pituitary problems from acquired causes (such as tumors, surgery, infection, or trauma) are unlikely to benefit directly from these genetic discoveries.

Why it matters

Potential benefit: If successful, this work could help more people with congenital pituitary hormone deficiencies get a genetic diagnosis to guide care and predict future risks.

How similar studies have performed: Mouse-based gene discovery has already identified many causes of congenital hypopituitarism, so this approach builds on proven methods even though many patients still lack a diagnosis.

Where this research is happening

ANN ARBOR, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Anterior Pituitary Hyposecretion Syndrome

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.