Exploring a new treatment target for acute myeloid leukemia

Discovery of a novel MDM2-tubulin signaling pathway as a therapeutic target in AML

NIH-funded research Emory University · NIH-10991670

This study is exploring a new way to treat acute myeloid leukemia (AML) by looking at how a specific gene and a protein work together, and it’s testing a promising drug called VERU-111 that could help kill AML cells while being gentler on the body.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionEmory University NIH-funded
Lab location1 site (Atlanta, United States)
Project IDNIH-10991670 on NIH RePORTER

What this research studies

This research investigates a novel signaling pathway involving the MDM2 oncogene and tubulin, aiming to develop targeted therapies for acute myeloid leukemia (AML). The approach focuses on a specific inhibitor, VERU-111, which has shown promise in selectively killing AML cells with high MDM2 expression without activating p53, a common tumor suppressor. By understanding how MDM2 interacts with tubulin, the research seeks to create more effective and less toxic treatment options for patients suffering from AML. The study will involve laboratory experiments and potentially lead to clinical trials for new therapies.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with acute myeloid leukemia, particularly those with high levels of MDM2 expression.

Not a fit: Patients with other types of leukemia or those who do not express high levels of MDM2 may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective and less toxic treatments for patients with acute myeloid leukemia.

How similar studies have performed: Other research has shown success with targeted therapies in cancer treatment, making this approach promising but still relatively novel in the context of AML.

Where this research is happening

Atlanta, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.