Evaluating the use of off-label drugs for heart conditions in children and adolescents

Off-label drugs in cardiology: evaluating age- and disease-appropriate therapies

NIH-funded research Children's Research Institute · NIH-11037904

This study is looking at how well certain medications, not usually approved for kids, work for children with heart problems, especially those born with heart defects, to make sure they get the safest and most effective treatments for their age.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionChildren's Research Institute NIH-funded
Lab location1 site (Washington, United States)
Project IDNIH-11037904 on NIH RePORTER

What this research studies

This research investigates the use of off-label medications in treating pediatric patients with cardiovascular diseases, particularly those with congenital heart disease. It aims to understand how age and disease impact the effectiveness and safety of these medications, as many children receive treatments not specifically approved for their age group. The study will utilize innovative techniques to assess how immature heart physiology affects drug responsiveness, ensuring that therapies are tailored to the unique needs of younger patients. By focusing on age-appropriate therapies, the research seeks to improve treatment outcomes for children and adolescents with heart conditions.

Who could benefit from this research

Good fit: Ideal candidates for this research include children and adolescents with congenital heart disease or other cardiovascular conditions requiring medication.

Not a fit: Patients who are adults or those without cardiovascular conditions may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to safer and more effective heart treatments specifically designed for children and adolescents.

How similar studies have performed: Previous research has shown that tailored approaches to medication in pediatric populations can lead to improved outcomes, indicating potential success for this innovative approach.

Where this research is happening

Washington, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.