Developing targeted therapies for children with RAS-driven rhabdomyosarcoma

Improving Therapeutic Approaches for RAS-driven Rhabdomyosarcoma

['FUNDING_R37'] · OREGON HEALTH & SCIENCE UNIVERSITY · NIH-11013863

This study is working to find better and safer treatments for kids with a tough type of cancer called high-risk rhabdomyosarcoma, especially those with certain gene changes, by exploring new drug combinations that could help them fight the disease more effectively.

Quick facts

Phase['FUNDING_R37']
Study typeNih_funding
SexAll
SponsorOREGON HEALTH & SCIENCE UNIVERSITY (nih funded)
Locations1 site (PORTLAND, UNITED STATES)
Trial IDNIH-11013863 on ClinicalTrials.gov

What this research studies

This research focuses on improving treatment options for children diagnosed with high-risk rhabdomyosarcoma (RMS), particularly those with RAS mutations. The project aims to create less harmful, targeted therapies that can effectively combat this aggressive cancer, which has shown poor survival rates despite current treatments. By investigating the mechanisms of resistance to existing therapies, the researchers hope to develop new combinations of drugs that can lead to better outcomes for young patients. The approach includes innovative testing methods to evaluate the effectiveness of these new treatments in preclinical models.

Who could benefit from this research

Good fit: Ideal candidates for this research are children aged 0-11 years who have been diagnosed with high-risk rhabdomyosarcoma, particularly those with RAS mutations.

Not a fit: Patients with rhabdomyosarcoma who do not have RAS mutations or who are outside the age range of 0-11 years may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective and less toxic treatment options for children suffering from RAS-driven rhabdomyosarcoma.

How similar studies have performed: Other research has shown promise in targeting the MAPK pathway for similar cancers, indicating that this approach may lead to significant advancements in treatment.

Where this research is happening

PORTLAND, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: cancer chemotherapy

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.