Developing methods for manufacturing a new drug.
SLAUGENHAUPT-MGH DMFP FOR BPN36964 (PTC680)
This study is working on developing a new drug called BPN36964 (PTC680) to help patients who need better treatment options, making sure it's safe and effective through careful testing.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Midwest Research Institute NIH-funded |
| Lab location | 1 site (Kansas City, United States) |
| Project ID | NIH-10949228 on NIH RePORTER |
What this research studies
This research focuses on creating and validating the analytical methods necessary for the production of a new drug, BPN36964 (PTC680). The approach involves ensuring that the manufacturing process meets safety and quality standards through rigorous testing and qualification of the methods used. Patients may benefit from this research as it aims to support the development of a new treatment option that could address unmet medical needs. The research will involve collaboration with various stakeholders to ensure that the drug is produced effectively and safely.
Who could benefit from this research
Good fit: Ideal candidates for participation would be those who are affected by conditions that may be treated by the new drug being developed.
Not a fit: Patients who do not have conditions that the new drug targets may not receive any benefit from this research.
Why it matters
Potential benefit: If successful, this research could lead to the availability of a new treatment option for patients.
How similar studies have performed: While the specific drug and methods are novel, similar approaches in drug development have shown success in bringing new treatments to market.
Where this research is happening
Kansas City, United States
- Midwest Research Institute — Kansas City, United States (Active)
Researchers
- Principal investigator: Penny, Brian — Midwest Research Institute
- Study coordinator: Penny, Brian
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page below.