Creating new treatments using genome editing for genetic diseases
Dissemination and Coordinating Center for the SCGE Consortium
This study is working on new ways to use gene editing to help treat people with both rare and common genetic diseases, and it aims to bring researchers together to share ideas and tools so that patients can get better treatments for their specific conditions.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Medical College of Wisconsin NIH-funded |
| Lab location | 1 site (Milwaukee, United States) |
| Project ID | NIH-10531271 on NIH RePORTER |
What this research studies
This research aims to develop and promote innovative genome editing technologies that can be used to treat both rare and common genetic diseases. The project will establish a central hub for collaboration among researchers, facilitating communication and data sharing to enhance the development of new therapeutic strategies. By building a comprehensive toolkit and infrastructure, the initiative seeks to streamline the process of testing and implementing these groundbreaking treatments in clinical settings. Patients may benefit from advancements in therapies that target their specific genetic conditions.
Who could benefit from this research
Good fit: Ideal candidates for this research include individuals with rare genetic diseases or common genetic disorders who may benefit from innovative genome editing therapies.
Not a fit: Patients with non-genetic diseases or those whose conditions are not related to genetic factors may not receive any benefit from this research.
Why it matters
Potential benefit: If successful, this research could lead to new, effective treatments for patients suffering from genetic disorders.
How similar studies have performed: Previous research in genome editing has shown promising results, indicating that this approach has the potential to significantly impact treatment options for genetic disorders.
Where this research is happening
Milwaukee, United States
- Medical College of Wisconsin — Milwaukee, United States (Active)
Researchers
- Principal investigator: Dwinell, Melinda R — Medical College of Wisconsin
- Study coordinator: Dwinell, Melinda R
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page below.