Creating new mouse models to find treatments for cognitive issues in Down syndrome related to Alzheimer's disease

Generation and analysis of new mouse models to determine novel therapeutic targets for Down syndrome-associated cognitive deficits

['FUNDING_R01'] · ROSWELL PARK CANCER INSTITUTE CORP · NIH-10937797

This study is looking at how Alzheimer's disease impacts thinking and memory in people with Down syndrome, using specially modified mice to find new ways to help improve their cognitive abilities.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorROSWELL PARK CANCER INSTITUTE CORP (nih funded)
Locations1 site (BUFFALO, UNITED STATES)
Trial IDNIH-10937797 on ClinicalTrials.gov

What this research studies

This research focuses on understanding the complex relationship between Down syndrome and Alzheimer's disease, particularly how Alzheimer's affects cognitive function in individuals with Down syndrome. Using advanced CRISPR technology, researchers will create genetically modified mice to study the roles of specific proteins involved in Alzheimer's pathology. By investigating these molecular mechanisms, the goal is to identify potential therapeutic targets that could lead to effective treatments for cognitive deficits associated with Down syndrome and Alzheimer's disease.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals with Down syndrome, particularly those who are at risk of developing Alzheimer's disease as they age.

Not a fit: Patients without Down syndrome or those who do not have cognitive deficits related to Alzheimer's disease may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new therapies that improve cognitive function and quality of life for individuals with Down syndrome who are affected by Alzheimer's disease.

How similar studies have performed: Previous research has shown promise in using genetic models to explore Alzheimer's disease mechanisms, indicating that this approach could yield valuable insights.

Where this research is happening

BUFFALO, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Alzheimer Disease 1 Protein, Alzheimer Disease Protease Nexin-II, Alzheimer disease dementia

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.