Creating a new rat model to study a rare genetic brain disease

Novel Knock in Mutation Rat Model for CARASIL

NIH-funded research University of Rhode Island · NIH-10518554

This study is creating a special type of rat to help us learn more about a rare brain condition called CARASIL, so we can better understand how it affects thinking and movement, and hopefully find new ways to help people with this disease.

Quick facts

Grant typeR21 grant
Study typeNIH-funded research
Funding institutionUniversity of Rhode Island NIH-funded
Lab location1 site (Kingston, United States)
Project IDNIH-10518554 on NIH RePORTER

What this research studies

This research focuses on developing a novel rat model to investigate cerebral small vessel diseases (CSVD), particularly a rare condition known as CARASIL. By using genetic modifications, the researchers aim to replicate the disease's characteristics in rats, which will help in understanding its progression and effects on cognitive function. The study will utilize advanced imaging techniques to observe brain changes and assess the impact of the disease on behavior and motor skills. This model could provide valuable insights into potential treatments and interventions for affected individuals.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with CARASIL or those exhibiting symptoms of cerebral small vessel diseases.

Not a fit: Patients with other forms of dementia or cognitive impairment unrelated to CSVD may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to better understanding and treatment options for patients suffering from CARASIL and related cognitive impairments.

How similar studies have performed: While research on CSVD is ongoing, the specific approach of creating a novel rat model for CARASIL is relatively novel and has not been extensively tested in prior studies.

Where this research is happening

Kingston, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.