Coordination of a gene therapy program for personalized treatments
Official title: NATIONAL INSTITUTE OF HEALTH (NIH), NATIONAL CENTER FOR ADVANCING TRANSLATIONAL SCIENCES (NCATS), BESPOKE GENE THERAPY CONSORTIUM - COORDINATION CENTER
Funded at Black Canyon Consulting LLC · NIH-10950099 · Data updated 2026-11-12
This study is all about bringing together experts to create personalized gene therapies that could help patients with specific genetic conditions, making sure everyone works well together to develop these innovative treatments.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Black Canyon Consulting LLC NIH-funded |
| Lab location | 1 site (Fairfax, United States) |
| Project start | September 1, 2023 |
| Project end | August 31, 2026 |
| Funding year | 2023 |
| Award (this year) | $2,234,205 |
| NIH project number | 75N98022D00019-0-759802300006-1 |
| Project ID | NIH-10950099 on NIH RePORTER |
Who could benefit from this research
✓Could help
Ideal candidates for participation would include individuals with specific genetic conditions that may be addressed through bespoke gene therapies.
✕Less likely to help
Patients with conditions that are not targeted by the gene therapy projects or those who do not have genetic disorders may not receive any benefit from this research.
What this research studies
This research focuses on managing and coordinating activities for the Bespoke Gene Therapy Consortium, which aims to develop personalized gene therapies. The project involves establishing a Program Management Office to oversee various core activities and ensure effective collaboration among clinical development teams. Patients may benefit from advancements in gene therapy tailored to their specific genetic conditions, as the consortium works on innovative treatment approaches. The research emphasizes the importance of expert resources and project management in facilitating successful gene therapy projects.
Why it matters
Potential benefit: If successful, this research could lead to the development of personalized gene therapies that improve treatment outcomes for patients with genetic disorders.
How similar studies have gone: Previous research in gene therapy has shown promising results, indicating that personalized approaches can lead to significant advancements in treatment efficacy.
Where this research is happening
-
Black Canyon Consulting LLC
Fairfax, United States Active
Related research
Other NIH-funded projects on the same topics.
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Developing tools to fight antibiotic-resistant bacteria
This study is working on improving online tools that help scientists and doctors find and understand antibiotic-resistant bacteria, so they can better tackle infections that are hard to treat.
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Coordination of a gene therapy program focused on adeno-associated viruses.
This study is all about working together to create new gene therapies that could help people with genetic disorders, so if you're looking for exciting new treatment options, this could be for you!
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.