Combining DNA-repair blocker drugs with chemotherapy for glioblastoma

Novel DNA damage response inhibitor and alkylator combinations for GBM

NIH-funded research Mayo Clinic Rochester · NIH-11189643

This project combines drugs that block DNA-repair (ATM/ATR inhibitors) with alkylating chemotherapy to try to better kill glioblastoma brain tumors.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionMayo Clinic Rochester NIH-funded
Lab location1 site (Rochester, United States)
Project IDNIH-11189643 on NIH RePORTER

What this research studies

Researchers are testing whether drugs that block the ATM and ATR DNA-repair proteins can make standard alkylating chemotherapies like temozolomide work better against glioblastoma. They will use lab and preclinical models and partner with pharmaceutical companies to study brain-penetrant ATM and ATR inhibitors in combination with alkylators and radiation. The team already has early lab evidence showing strong synergy between temozolomide and ATR inhibitors in glioblastoma models. If this work translates, it could move these combinations into clinical trials for patients.

Who could benefit from this research

Good fit: Adults with newly diagnosed or recurrent glioblastoma who are receiving or eligible for alkylating chemotherapy (for example temozolomide) would be the likely candidates.

Not a fit: People with other types of brain tumors, those not eligible for chemotherapy, or patients with medical conditions that prevent use of ATM/ATR inhibitors may not benefit.

Why it matters

Potential benefit: If successful, this approach could make standard chemotherapy more effective against glioblastoma and help control tumor growth longer.

How similar studies have performed: Preclinical studies and collaborations with the NCI and pharma have shown promising synergy between temozolomide and ATR inhibitors in lab models, but clear benefit in patients has not yet been established.

Where this research is happening

Rochester, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.