Cell and genetic causes of keratoconus

Cellular and Genetic Defects in Keratoconus

NIH-funded research New York University School of Medicine · NIH-11262821

Researchers are analyzing cell changes and genes in people with keratoconus to find early warning signs and new treatment targets.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionNew York University School of Medicine NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11262821 on NIH RePORTER

What this research studies

This project studies corneas and DNA from people with keratoconus and their families to find the cellular problems and genetic changes that lead to corneal thinning and scarring. The team uses whole-exome sequencing of families plus transcriptomic and proteomic analysis of donated corneal tissue to find rare gene variants and disrupted pathways. They are especially focused on cell-stress, cytoskeleton, and extracellular matrix genes and on a weakened antioxidant (NRF2) response seen in affected corneas. The goal is to link genetic findings with tissue-level changes to discover biomarkers and potential therapeutic targets.

Who could benefit from this research

Good fit: Ideal participants include people diagnosed with keratoconus, especially those willing to provide clinical data, family members for genetic studies, or donors of corneal tissue.

Not a fit: People without keratoconus or those needing immediate surgical correction should not expect direct, immediate benefit from this research.

Why it matters

Potential benefit: If successful, this work could enable earlier diagnosis through biomarkers and point to new treatments that slow or prevent vision loss from keratoconus.

How similar studies have performed: Previous genetic and tissue studies have identified some candidate genes and corneal pathway changes, but combining family exome sequencing with detailed tissue proteomics and transcriptomics is a more comprehensive and newer approach.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.