Cathepsin L's role in changing nuclear proteins linked to aging and Alzheimer’s

Cathepsin-L mediated remodeling of the nuclear proteome

NIH-funded research Saint Louis University · NIH-11231249

Seeing if changing levels of the enzyme cathepsin L can reduce harmful nuclear proteins in people with Alzheimer’s disease and premature-aging syndromes.

Quick facts

Grant typeR21 grant
Study typeNIH-funded research
Funding institutionSaint Louis University NIH-funded
Lab location1 site (Saint Louis, United States)
Project IDNIH-11231249 on NIH RePORTER

What this research studies

This project looks at an enzyme called cathepsin L that can alter proteins inside the cell nucleus that are linked to aging and Alzheimer’s. Researchers will work with patient-derived cells (including cells from people with progeria) and lab experiments to see how cathepsin L trims or remodels nuclear proteins such as lamin B1 and progerin. They will test whether drugs like chloroquine that raise nuclear cathepsin L levels reduce toxic protein fragments and signs of cellular aging. The goal is to identify molecular steps that could become targets for future treatments to protect brain cells or reduce damage in rare premature-aging conditions.

Who could benefit from this research

Good fit: Patients with Alzheimer’s disease or with Hutchinson–Gilford Progeria Syndrome (or their caregivers) would be most directly interested and could consider contributing biological samples in future related work.

Not a fit: People with conditions unrelated to nuclear lamins or those seeking immediate clinical therapies are unlikely to benefit directly from this early laboratory research.

Why it matters

Potential benefit: If successful, this work could point to new ways to reduce toxic nuclear proteins and potentially slow progression of Alzheimer’s or lessen symptoms of progeria.

How similar studies have performed: Prior laboratory studies showed that raising nuclear cathepsin L improved cellular features in progeria cells and similar nuclear changes are seen in Alzheimer’s, but this approach has not yet produced proven treatments for people.

Where this research is happening

Saint Louis, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Alzheimer disease dementiaAlzheimer syndromeAlzheimer's Disease
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.