Brainstem Phox2b cells that sense CO2 and control breathing

Molecular physiology of Phox2b-expressing RTN chemoreceptor neurons

NIH-funded research University of Virginia · NIH-11312615

This project looks at how the Phox2b gene keeps CO2-sensing brainstem cells working so people with breathing disorders like congenital central hypoventilation syndrome (CCHS) might benefit.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Virginia NIH-funded
Lab location1 site (Charlottesville, United States)
Project IDNIH-11312615 on NIH RePORTER

What this research studies

You'll learn that researchers use mouse genetic models and viral tools to change Phox2b in tiny CO2-sensing brainstem neurons called the retrotrapezoid nucleus (RTN). They compare normal Phox2b with CCHS-like mutations to find which genes those neurons need to drive breathing and arousal. The team measures breathing and wakefulness responses and maps how RTN neurons connect with other brain centers. Together, these steps aim to reveal biological targets that could guide future treatments or diagnostics.

Who could benefit from this research

Good fit: People with congenital central hypoventilation syndrome (CCHS) or families affected by unexplained infant sleep-related deaths (SIDS) would be most directly relevant to this work and to future related studies.

Not a fit: People whose breathing problems are caused primarily by lung disease, obstructive sleep apnea, neuromuscular disorders, or other non-brainstem causes are less likely to benefit from findings focused on Phox2b/RTN neurons.

Why it matters

Potential benefit: If successful, this work could identify genes and pathways to guide new diagnostics or therapies for CCHS and related breathing–arousal disorders.

How similar studies have performed: Previous mouse genetic studies have shown Phox2b mutations disrupt RTN development and breathing, so this builds on established animal models while applying newer viral and genomic tools to study postnatal gene function.

Where this research is happening

Charlottesville, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Candidate Disease Gene
Last reviewed 2026-06-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.