Boosting cetuximab response in oral cancer by targeting mitochondrial complex I

Inhibiting mitochondrial complex I to improve cetuximab efficacy in oral cancer

['FUNDING_R01'] · EMORY UNIVERSITY · NIH-11322613

This work tries adding a drug that blocks a mitochondrial enzyme to help cetuximab work better for people with oral squamous cell carcinoma.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorEMORY UNIVERSITY (nih funded)
Locations1 site (ATLANTA, UNITED STATES)
Trial IDNIH-11322613 on ClinicalTrials.gov

What this research studies

Researchers are using lab-grown oral cancer cells and a mouse model that carries human EGFR to see whether a pill called IACS-010759, which blocks mitochondrial complex I, can make cetuximab kill more tumor cells. They used a genome-wide CRISPR screen to find that TNFα signaling helps tumors survive cetuximab and found that IACS redirects that signal to trigger inflammatory cell death (pyroptosis) via ROS and gasdermin D. The team also examines how CD8+ T cells contribute to tumor remission when the two drugs are combined. These preclinical experiments aim to generate evidence that could support future clinical testing of the combination in patients.

Who could benefit from this research

Good fit: Ideal candidates would be adults with EGFR-expressing oral squamous cell carcinoma who are eligible for cetuximab therapy or have tumors that are resistant to it.

Not a fit: People whose tumors do not express EGFR, who cannot tolerate mitochondrial complex I inhibitors, or who have unrelated serious health issues may not benefit from this approach.

Why it matters

Potential benefit: If successful, this approach could make cetuximab effective for more people with oral squamous cell carcinoma and stimulate immune-mediated tumor clearance.

How similar studies have performed: Mitochondrial complex I inhibitors like IACS-010759 have shown anti-cancer activity in laboratory and animal studies, but combining them with cetuximab for oral cancer is a novel, mostly preclinical strategy.

Where this research is happening

ATLANTA, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.