Allopregnanolone for Brain Regeneration in Alzheimer's Disease

Allopregnanolone as Regenerative Therapeutic for Alzheimer's: Phase 2 Clinical Trial

NIH-funded research University of Arizona · NIH-10851927

This research explores if a natural brain compound called allopregnanolone can help regenerate brain cells and improve memory for people with early Alzheimer's disease.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Arizona NIH-funded
Lab location1 site (Tucson, United States)
Project IDNIH-10851927 on NIH RePORTER

What this research studies

We are exploring a new way to help the brain heal itself and reduce the effects of Alzheimer's disease. This approach uses allopregnanolone, a natural substance in the brain, which has shown promise in laboratory and animal models by helping new brain cells grow and improving thinking abilities. We believe this compound can also lessen the harmful changes seen in Alzheimer's. A previous small study found that this treatment was safe and well-tolerated, with no significant side effects.

Who could benefit from this research

Good fit: Ideal candidates are individuals diagnosed with mild cognitive impairment (MCI) due to Alzheimer's or early-stage Alzheimer's disease.

Not a fit: Patients with advanced Alzheimer's disease or other forms of dementia may not receive benefit from this specific approach.

Why it matters

Potential benefit: If successful, this treatment could help restore brain function and slow the progression of Alzheimer's disease.

How similar studies have performed: Preclinical studies have shown promising results in animal models, and a previous Phase 1 clinical trial indicated the treatment was safe and well-tolerated in humans.

Where this research is happening

Tucson, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Alzheimer disease dementia
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.