Age-appropriate heart medication strategies for children with congenital heart disease

Off-label drugs in cardiology: evaluating age- and disease-appropriate therapies

NIH-funded research Children's Research Institute · NIH-11285264

This work looks at how common heart medicines affect babies, children, and teens so doctors can choose safer, age-tailored treatments.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionChildren's Research Institute NIH-funded
Lab location1 site (Washington, United States)
Project IDNIH-11285264 on NIH RePORTER

What this research studies

As a parent or patient, this project focuses on how developing hearts in newborns, infants, children, and adolescents respond differently to medications often prescribed off-label for congenital heart disease. The team will study age-related differences in ion channels, calcium handling, and adrenergic drug targets using laboratory models that mimic immature myocardium alongside clinical data. Researchers will examine drugs commonly used in pediatric cardiac care—such as beta-blockers, antiarrhythmics, adrenergic agents, and calcium channel blockers—to understand variable effects and possible harms at different ages. The goal is to produce guidance that helps clinicians pick safer drugs and dosing for children before, during, and after heart surgery.

Who could benefit from this research

Good fit: Ideal candidates are newborns, infants, children, or adolescents with congenital heart disease who receive cardiovascular medications or are planning to undergo cardiac surgery.

Not a fit: People without congenital heart disease or adults whose treatment follows standard adult dosing guidelines are unlikely to directly benefit from this pediatric-focused work.

Why it matters

Potential benefit: If successful, this work could lead to safer, more effective drug choices and dosing for infants, children, and teens with congenital heart disease.

How similar studies have performed: Adult studies and some pediatric reports hint that age changes drug responses, but physiology-driven, pediatric-focused work of this scope is relatively novel.

Where this research is happening

Washington, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.