A network for conducting clinical trials in neuroscience
Clinical Research Sites for the Network of Excellence in Neuroscience Clinical Trials (NeuroNEXT sites) (U24 Clinical Trial Not Allowed)
This study is working to create a friendly network of places where people with ALS and other rare diseases can join early gene therapy trials, making it easier for everyone, especially those from underrepresented groups, to participate and get the help they need.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Columbia University Health Sciences NIH-funded |
| Lab location | 1 site (New York, United States) |
| Project ID | NIH-10886793 on NIH RePORTER |
What this research studies
This research focuses on establishing a network of clinical trial sites dedicated to neuroscience, particularly for conditions like amyotrophic lateral sclerosis (ALS) and other rare diseases. The team at Columbia University Medical Center and Weill Cornell Medical College has developed a robust infrastructure to facilitate early-phase gene therapy trials and improve participant recruitment, especially among underrepresented groups. They are also creating new tools to help identify eligible patients for these trials, ensuring a more inclusive approach to clinical research.
Who could benefit from this research
Good fit: Ideal candidates for participation include individuals diagnosed with ALS or other related neurological disorders, particularly those who are 21 years or older.
Not a fit: Patients with conditions unrelated to ALS or those under 21 years old may not benefit from this research.
Why it matters
Potential benefit: If successful, this research could lead to innovative treatments for ALS and other rare neurological conditions, improving patient outcomes.
How similar studies have performed: Previous research in gene therapy for neurological conditions has shown promise, indicating that this approach could yield significant advancements.
Where this research is happening
New York, United States
- Columbia University Health Sciences — New York, United States (Active)
Researchers
- Principal investigator: Marder, Karen S — Columbia University Health Sciences
- Study coordinator: Marder, Karen S
About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page below.