A brain-penetrating form of erythropoietin aimed at treating Alzheimer’s disease

Efficacy, safety, and mechanisms of brain penetrable erythropoietin in Alzheimer’s disease mouse models

NIH-funded research Chapman University · NIH-11300964

They are developing a modified erythropoietin that can enter the brain to protect nerve cells and help people with Alzheimer’s disease.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionChapman University NIH-funded
Lab location1 site (Orange, United States)
Project IDNIH-11300964 on NIH RePORTER

What this research studies

Researchers have attached erythropoietin (EPO) to an antibody that uses the transferrin receptor to cross the blood-brain barrier so more drug reaches the brain. In laboratory work with Alzheimer’s mouse models, the team gives this TfR‑antibody‑EPO fusion and measures effects on neuron survival, amyloid and tau pathology, and memory-related behaviors. They compare the fusion to regular EPO to check whether it reduces blood-related side effects while providing stronger brain benefits. The findings will be used to understand how the drug works and whether it is safe enough to consider future human trials.

Who could benefit from this research

Good fit: People living with Alzheimer's disease, especially those in early or mild stages who might be eligible for future clinical trials, would be the eventual candidates for this approach.

Not a fit: People without Alzheimer’s or those with very advanced, widespread brain damage are unlikely to benefit from this approach as tested in these early lab studies.

Why it matters

Potential benefit: If successful, this approach could lead to a treatment that protects brain cells and slows or reverses cognitive decline in people with Alzheimer's while minimizing blood-related side effects.

How similar studies have performed: Related brain-delivery approaches and EPO treatments have shown promise in animal models but have not yet been proven safe and effective in people.

Where this research is happening

Orange, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Acquired brain injury
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.