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Stargardt Disease 1 clinical trials and research
As of November 12, 2026, Find a Trial lists 3 Stargardt Disease 1 clinical trials that are recruiting, at sites in 3 countries (most in United States (1), China (1), Australia (1)). By phase: Phase 1/2 (1), Phase 1 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 3Clinical trials
- 3Countries
Newest Stargardt Disease 1 clinical trials
| Study | Phase | Where | Status | Registered |
|---|---|---|---|---|
| City-RBP4 in healthy people and Stargardt disease type 1 patients | Phase 1 | Melbourne, Victoria | Recruiting | Sep 23, 2026 |
| VG801 gene therapy for Stargardt disease from ABCA4 mutations | Phase 1/2 | Shanghai, Shanghai Municipality | Recruiting | Jun 3, 2025 |
| Identifying potential participants for Stargardt disease clinical trials | — | San Francisco, California and 8 other locations | Recruiting | Jun 6, 2024 |
All recruiting trials (3)
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City-RBP4 in healthy people and Stargardt disease type 1 patients
This first-in-human study tests CITY-RBP4 to see if it is safe and how it behaves in the body for healthy volunteers and people with Stargardt disease type 1.
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VG801 gene therapy for Stargardt disease from ABCA4 mutations
This open-label, first-in-human trial will try a single dose of VG801 gene therapy in people aged 6 and older who have Stargardt disease from two ABCA4 mutations to see if it is safe and helps vision.
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Identifying potential participants for Stargardt disease clinical trials
This study is trying to find people with Stargardt disease who might qualify for upcoming clinical trials by checking if they meet certain criteria, like having specific gene mutations.
Related topics
Quick answers
How many Stargardt Disease 1 clinical trials are recruiting right now?
3, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in United States (1 trial), China (1 trial), Australia (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1, Phase 1: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.