Condition
OPA1 Gene Mutation clinical trials and research
As of November 12, 2026, Find a Trial lists 2 OPA1 Gene Mutation clinical trials that are recruiting, at sites in 3 countries (most in Germany (1), Australia (1), New Zealand (1)). By phase: Phase 1/2 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 3Countries
All recruiting trials (2)
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Long-term picture of OPA1-related optic atrophy in kids and adults
This study follows people with an OPA1 gene change to see how their optic nerve disease progresses over time.
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PYC-001 eye injections for people with OPA1-related autosomal dominant optic atrophy
This trial tests whether injections of PYC-001 into one eye are safe and what dosing schedule works best for adults with OPA1 mutation–related autosomal dominant optic atrophy.
Quick answers
How many OPA1 Gene Mutation clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 3 countries. The most sites are in Germany (1 trial), Australia (1 trial), New Zealand (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.