Condition
Glycogen Storage Disease Type II clinical trials and research
As of November 12, 2026, Find a Trial lists 2 Glycogen Storage Disease Type II clinical trials that are recruiting, at sites in 37 countries (most in China (2), Argentina (1), Australia (1)). By phase: Phase 4 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 37Countries
All recruiting trials (2)
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Avalglucosidase alfa treatment for children with Pompe disease
This study is testing a new treatment called avalglucosidase alfa to see if it helps children with infantile-onset Pompe disease feel better over a year.
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Global registry for tracking Pompe disease outcomes
This study is tracking the health and progress of people with Pompe disease to learn more about how it affects them and to see how well treatments are working.
Related topics
Quick answers
How many Glycogen Storage Disease Type II clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 37 countries. The most sites are in China (2 trials), Argentina (1 trial), Australia (1 trial), Belgium (1 trial), Brazil (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 4: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.