Condition

Glycogen Storage Disease Type Ia clinical trials and research

• 4Clinical trials
• 9Countries

Newest Glycogen Storage Disease Type Ia clinical trials

All recruiting trials (4)

• Home lactate and Accu‑Chek glucose meter accuracy for people with glycogen storage disease

  This project will see if a handheld Lactate Plus meter and an Accu‑Chek glucometer give results that match lab blood tests in people with glycogen storage disease types Ia, Ib, and XI.

  Recruiting Connecticut Children's Medical Center · Hartford, Connecticut · NCT07459582

• Evaluating the accuracy of home lactate meters in patients with Glycogen Storage Disease Type Ia

  This study tests if home lactate meters give accurate readings for people with Glycogen Storage Disease Type Ia by comparing them to lab results.

  Recruiting Connecticut Children's Medical Center · Hartford, Connecticut · NCT06843330

• Evaluating BEAM-301 for treating Glycogen Storage Disease Type Ia

  This study is testing a new treatment called BEAM-301 to see if it is safe and effective for adults with Glycogen Storage Disease Type Ia who have a specific genetic variant.

  Recruiting at 3 sites Phase 1/2 Beam Therapeutics Inc. · Orange, California and 2 other locations · NCT06735755

• Monitoring program for patients with Glycogen Storage Disease Type Ia

  This study is tracking the long-term health and safety of a treatment called DTX401 in people with Glycogen Storage Disease Type Ia to see how it helps them over at least 10 years.

  Recruiting at 17 sites Ultragenyx Pharmaceutical Inc · Orange, California and 18 other locations · NCT06636383

Related topics

Quick answers

How many Glycogen Storage Disease Type Ia clinical trials are recruiting right now?

4, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.

Where are these trials running?

In 9 countries. The most sites are in United States (4 trials), Brazil (1 trial), Canada (1 trial), Denmark (1 trial), Germany (1 trial). Each study page lists its sites and which ones are recruiting.

What phases are they in?

Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.

How do I join one?

Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.

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