Condition
CTNNB1 Neurodevelopmental Syndrome clinical trials and research
As of November 12, 2026, Find a Trial lists 2 CTNNB1 Neurodevelopmental Syndrome clinical trials that are recruiting, at sites in 2 countries (most in Slovenia (2), Australia (1)). By phase: Phase 1/2 (1). Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 2Clinical trials
- 2Countries
All recruiting trials (2)
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Urbagen gene replacement for children with CTNNB1 neurodevelopmental syndrome
This trial will try a one-time AAV9 gene replacement called Urbag en, delivered into the brain, to see if it is safe and helps children aged 2–12 with CTNNB1 neurodevelopmental syndrome.
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Tracking development in people with CTNNB1 neurodevelopmental syndrome
The team will see how CTNNB1 gene changes affect development over time in children and adults with CTNNB1 neurodevelopmental syndrome.
Quick answers
How many CTNNB1 Neurodevelopmental Syndrome clinical trials are recruiting right now?
2, as of November 12, 2026. We update this list each time we refresh our data from ClinicalTrials.gov.
Where are these trials running?
In 2 countries. The most sites are in Slovenia (2 trials), Australia (1 trial). Each study page lists its sites and which ones are recruiting.
What phases are they in?
Phase 1/2: 1. Trials with no phase listed are usually device, behavioural or observational studies.
How do I join one?
Open a study, check the "Is this trial a fit for you?" section, then contact the study team listed on the page. They will ask a few screening questions. Asking is free and does not commit you to anything. Talk it over with your doctor first.
Find the studies that fit you
A list is a starting point. Tell us your situation in your own words and we'll rank the studies that match and explain why. It's free and needs no account.